A Year After Gene Therapy, Boys With Muscular Dystrophy Are Healthier and Stronger

Good News Notes: “Two and a half years ago, a study published in Science Advances detailed how the gene editing tool CRISPR/Cas-9 repaired genetic mutations related to Duchenne Muscular Dystrophy (DMD). The study was a proof of concept, and used induced pluripotent stem cells (iPSCs). But now a similar treatment has not only been administered to real people, it has…